Some of the most expensive drugs currently in use are gene therapies to treat specific diseases, and their high cost limits ...

A West Coast biotech entrepreneur says he’s secured $30 million to form a public-benefit company to study how to safely create genetically edited babies, marking the largest known investment into the ...

The trial was small — just 12 children were treated in one or both ears — but it offers important lessons for researchers about the potential of Regeneron’s gene therapy.

In many cells of the human body, hair-like protrusions known as cilia act as antennae, allowing cells to receive signals from ...

In a world first, a bespoke gene-editing therapy benefitted one child. Now reseachers plan to launch a clinical trial of the ...

Researchers at Fujita Health University and the Tokyo Metropolitan Institute of Medical Science have uncovered a previously overlooked form of brain abnormality linked to anxiety: excessive maturation ...

Researchers have identified molecular mechanisms behind age-related memory decline — and shown they can be reversed.

The Fast-Twitch Gene You Didn't Know You Had Your DNA might be giving you an edge or could be holding you back. The ACTN3 ...

MIT researchers discovered that the genome’s 3D structure doesn’t vanish during cell division as previously thought. Instead, ...

A study led by UCLA Health Jonsson Comprehensive Cancer Center investigators reveals how melanoma, the deadliest form of skin ...

The Byrds had a seemingly endless revolving door of musicians come and go over the years, but Gene Parsons was among the most ...

A study volunteer receiving Intellia’s transthyretin amyloidosis treatment was hospitalized due to severe signs of liver ...