Duke Eye Center has become the first academic medical center in the country to implant a new cell-based gene therapy for a rare eye disease called MacTel. This procedure offers hope to patients like ...

LONDON -- A 3-year-old girl who underwent a breakthrough gene therapy treatment to treat profound hearing loss can hear on ...

On her mother’s instruction, a toddler gives her pink stuffed horse, Snap Snap, a big cuddle. Then, as told, she plants a kiss on his soft fur and, because he’s hungry, feeds him a pretend bowl of ...

Up to 60% of congenital and early-onset hearing loss is caused by genetic mutations in an inherited gene, and gene therapy ...

ZEVASKYN ® (prademagene zamikeracel) is an autologous cell sheet-based gene therapy indicated for the treatment of wounds in ...

A one-time subretinal injection of Sura-vec at both high- and low-dose concentrations allowed more than half of patients with ...

We are now in the second great wave of the genetic revolution, not defined by reading the human code of life, but by rewriting it.

A groundbreaking gene therapy has successfully restored immune function in children with ADA-SCID, a severe genetic disorder. Developed by international researchers, the treatment corrected faulty ...

Researchers announce breakthrough results for AMT-130, the first disease-modifying treatment for Huntington's disease, with ...

These results are what we hoped for when we first began developing this approach,' one researcher said. View on euronews ...

Lilly’s upfront offer for Adverum, the developer of a gene therapy for age-related macular degeneration, is less than the ...

Gene therapy achieved its first major breakthroughs in the early 1990s with the treatment of a rare disease called severe combined immunodeficiency. However, the field was dealt a serious setback in ...